We the Scientists
How a Daring Team of Parents and Doctors Forged a New Path for Medicine
New York : Riverhead Books, 2023.
Format: Book
Edition: First edition.
Description: xxx, 222 pages ; 22 cm
"Pulitzer Prize-winning reporter Amy Dockser Marcus shows what happened when a group of parents joined forces with doctors and researchers to try to save children's lives. Parents whose children had been diagnosed with the rare and fatal genetic condition Niemann-Pick Type C disease recognized there would never be a treatment in time to save their children if things stayed the same, so the parents set up a collaboration with researchers and doctors in search of a cure. Their social experiment reveals new pathways for treating disease and conducting research"-- Provided by publisher.
Subjects:
Niemann-Pick diseases -- Treatment.
Rare diseases -- Patients.
Genetic disorders in children -- Patients -- Family relationships.
Parents of children with disabilities.
Niemann-Pick diseases -- Treatment.
Rare diseases -- Patients.
Genetic disorders in children -- Patients -- Family relationships.
Parents of children with disabilities.
ISBN:
9780399576133
Availability | |||
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Call Number | Location | Shelf Location | Status |
PARENTING Health Mar | Sandhills Indoors | Nonfiction | In |
Includes bibliographical references and index.